Sarepta Therapeutics

Latest clinical program signals indexed for Sarepta Therapeutics.

1. ARODM1-1001 — Phase 2

   Jun 8, 2026
   Clinical update →

2. SRP-9003-301 — Phase 3

   Jun 8, 2026
   Clinical update →

3. SRP-9001-303 — Phase 3

   Jun 8, 2026
   Clinical update →

4. SRP-9001-104 — Phase 1

   Jun 8, 2026
   Clinical update →

5. 4045-301 — Phase 3

   Jun 8, 2026
   Clinical update →

6. Delandistrogene moxeparvovec-rokl — Phase 3

   Jun 8, 2026
   Clinical update →

7. VESLETEPLIRSEN(SRP-5051) — Phase 2

   Jun 8, 2026
   Clinical update →

8. SODIUM CHLORIDE, ARO-DUX4 — Phase 2

   Jun 8, 2026
   Clinical update →

1. 2022-503112-17-00

   SRP-9003-301

   Phase 3 · active · small_molecule

   Limb-girdle muscular dystrophy, type 2E/R4 (LGMD2E/R4) or β-sarcoglycanopathy

   CTIS ↗
2. 2023-505043-39-00

   Delandistrogene moxeparvovec-rokl

   Phase 3 · active · small_molecule

   Duchenne Muscular Dystrophy

   CTIS ↗
3. 2023-509748-89-00

   SODIUM CHLORIDE, ARO-DUX4

   Phase 2 · active · small_molecule

   Facioscapulohumeral muscular dystrophy (FSHD)

   CTIS ↗
4. 2023-509935-23-00

   VESLETEPLIRSEN(SRP-5051)

   Phase 2 · active · small_molecule

   Duchenne Muscular Dystrophy

   CTIS ↗
5. 2024-511492-15-00

   ETEPLIRSEN (AVI-4658)

   Phase 3 · active · small_molecule

   Duchenne Muscular Dystrophy

   CTIS ↗
6. 2024-512624-11-00

   SRP-9001-104

   Phase 1 · active · small_molecule

   Duchenne muscular dystrophy (DMD)

   CTIS ↗
7. 2024-512626-28-00

   SRP-9001-303

   Phase 3 · active · small_molecule

   Duchenne Muscular Dystrophy

   CTIS ↗
8. 2024-513579-42-00

   ARODM1-1001

   Phase 2 · active · small_molecule

   Type 1 Myotonic Dystrophy

   CTIS ↗
9. 2024-514698-23-00

   4045-301

   Phase 3 · active · small_molecule

   Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Skipping.

   CTIS ↗
10. NCT00091845

    AVI-4020 Injection

    Phase 1 · terminated · small_molecule

    West Nile Fever

    CT.gov ↗
11. NCT00159250

    AVI-4658 (PMO)

    Phase 2 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
12. NCT00229749

    AVI-4065 Injection

    Phase 2 · terminated · small_molecule

    Hepatitis C

    CT.gov ↗
13. NCT00244647

    RESTEN-MP

    Phase 2 · completed · small_molecule

    Coronary Artery Disease

    CT.gov ↗
14. NCT00248066

    RESTEN-MP

    Phase 2 · completed · small_molecule

    Coronary Artery Disease

    CT.gov ↗
15. NCT00343148

    AVI-4126 Injection (RESTEN-NG®)

    Phase 1 · completed · small_molecule

    Neoplasms

    CT.gov ↗
16. NCT00381433

    AVI-4065 Injection

    Phase 1 · completed · small_molecule

    Encephalitis

    CT.gov ↗
17. NCT00387283

    AVI-4020 Injection

    Phase 1 · completed · small_molecule

    West Nile Virus

    CT.gov ↗
18. NCT00451256

    AVI-5126

    Phase 2 · terminated · small_molecule

    Cardiovascular Disease

    CT.gov ↗
19. NCT00844597

    AVI-4658 for Injection

    Phase 2 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
20. NCT01353027

    Placebo

    Phase 1 · completed · small_molecule

    Ebola Hemorrhagic Fever

    CT.gov ↗
21. NCT01353040

    AVI-6003

    Phase 1 · completed · small_molecule

    Marburg Hemorrhagic Fever

    CT.gov ↗
22. NCT01375985

    AVI-7100

    Phase 1 · terminated · small_molecule

    Influenza

    CT.gov ↗
23. NCT01396239

    AVI-4658 (Eteplirsen)

    Phase 2 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
24. NCT01540409

    AVI-4658 (Eteplirsen)

    Phase 2 · completed · small_molecule

    Duchenne Muscular Dystrophy (DMD)

    CT.gov ↗
25. NCT01566877

    AVI-7288

    Phase 1 · completed · small_molecule

    Marburg Hemorrhagic Fever

    CT.gov ↗
26. NCT01593072

    AVI-7537

    Phase 1 · terminated · small_molecule

    Ebola Hemorrhagic Fever

    CT.gov ↗
27. NCT01976091

    SRP-9004

    Phase 2 · completed · gene_therapy

    Limb-Girdle Muscular Dystrophy, Type 2D

    CT.gov ↗
28. NCT02255552

    eteplirsen

    Phase 3 · completed · small_molecule

    Duchenne Muscular Dystrophy (DMD)

    CT.gov ↗
29. NCT02286947

    Eteplirsen

    Phase 3 · active · small_molecule

    Muscular Dystrophy, Duchenne

    CT.gov ↗
30. NCT02310906

    Placebo

    Phase 2 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
31. NCT02420379

    eteplirsen

    Phase 3 · completed · small_molecule

    Duchenne Muscular Dystrophy (DMD)

    CT.gov ↗
32. NCT02500381

    SRP-4045

    Phase 3 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
33. NCT02530905

    SRP-4045

    Phase 3 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
34. NCT02710500

    rAAVrh74.MHCK7.DYSF.DV

    Phase 1 · completed · small_molecule

    Dysferlinopathy

    CT.gov ↗
35. NCT03218995

    Eteplirsen

    Phase 2 · terminated · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
36. NCT03375164

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
37. NCT03375255

    SRP-5051

    Phase 2 · terminated · small_molecule

    Muscular Dystrophy, Duchenne

    CT.gov ↗
38. NCT03532542

    Casimersen

    Phase 3 · terminated · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
39. NCT03652259

    SRP-9003

    Phase 2 · terminated · gene_therapy

    Limb-Girdle Muscular Dystrophy, Type 2E

    CT.gov ↗
40. NCT03675126

    SRP-5051

    Phase 2 · terminated · small_molecule

    Muscular Dystrophy, Duchenne

    CT.gov ↗
41. NCT03769116

    delandistrogene moxeparvovec

    Phase 2 · active · gene_therapy

    Muscular Dystrophy, Duchenne

    CT.gov ↗
42. NCT03985878

    Eteplirsen

    Phase 2 · terminated · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
43. NCT03992430

    Eteplirsen

    Phase 3 · active · small_molecule

    Muscular Dystrophy, Duchenne

    CT.gov ↗
44. NCT04004065

    Vesleteplirsen

    Phase 2 · terminated · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
45. NCT04179409

    Amondys 45

    Phase 2 · completed · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
46. NCT04626674

    delandistrogene moxeparvovec

    Phase 2 · active · gene_therapy

    Muscular Dystrophy, Duchenne

    CT.gov ↗
47. NCT04708314

    Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53]

    Approved · terminated · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗
48. NCT05096221

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
49. NCT05876780

    SRP-9003

    Phase 3 · active · mab

    Limb-girdle Muscular Dystrophy

    CT.gov ↗
50. NCT05881408

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
51. NCT05906251

    SRP-6004

    Phase 1 · terminated · gene_therapy

    Limb Girdle Muscular Dystrophy

    CT.gov ↗
52. NCT05967351

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
53. NCT06128564

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
54. NCT06241950

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
55. NCT06246513

    SRP-9003

    Phase 3 · active · mab

    Limb-girdle Muscular Dystrophy

    CT.gov ↗
56. NCT06597656

    delandistrogene moxeparvovec

    Phase 3 · active · gene_therapy

    Duchenne Muscular Dystrophy

    CT.gov ↗
57. NCT06747273

    SRP-9004

    Phase 1 · terminated · small_molecule

    Limb Girdle Muscular Dystrophy

    CT.gov ↗
58. NCT06952686

    SRP-9005

    Phase 3 · terminated · mab

    Muscular Dystrophies, Limb-Girdle

    CT.gov ↗
59. NCT07536061

    SRP-1005

    Phase 1 · active · small_molecule

    Huntington's Disease

    CT.gov ↗
60. NCT07542314

    ELEVIDYS

    Approved · active · small_molecule

    Duchenne Muscular Dystrophy

    CT.gov ↗