Friday, July 10, 2026

pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT

Sarepta Therapeutics

Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT · NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Clinical program

4045-301

Phase 3 · small molecule · Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Skipping.

4045-301 for Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Skipping. is a Phase 3 program (small_molecule) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).

← All Sarepta Therapeutics projects Phase 3 small molecule active

Internal code 4045-301

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Sarepta Therapeutics
Phase
Phase 3
Modality
small_molecule
Indication
Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Skipping.
Status
active
Trials
1