pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT
Sarepta Therapeutics
Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche
Company details
- Status
- Public
- HQ
- 215 First Street, Cambridge, MA 02142, US
- Employees
- 1,150
- Programs
- 46
- Drugs
- 23
- Patents
- 102
AVI-4658 (Eteplirsen)
Phase 2 · small molecule · Duchenne Muscular Dystrophy (DMD)
AVI-4658 (Eteplirsen) for Duchenne Muscular Dystrophy (DMD) is a Phase 2 program (small_molecule) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).
Internal code 4658-us-202
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- Sarepta Therapeutics
- Phase
- Phase 2
- Modality
- small_molecule
- Indication
- Duchenne Muscular Dystrophy (DMD)
- Status
- completed
- Trials
- 1