Wednesday, July 8, 2026

pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT

Sarepta Therapeutics

Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT · NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Clinical program

AVI-4658 (Eteplirsen)

Phase 2 · small molecule · Duchenne Muscular Dystrophy (DMD)

AVI-4658 (Eteplirsen) for Duchenne Muscular Dystrophy (DMD) is a Phase 2 program (small_molecule) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).

← All Sarepta Therapeutics projects Phase 2 small molecule completed

Internal code 4658-us-202

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Sarepta Therapeutics
Phase
Phase 2
Modality
small_molecule
Indication
Duchenne Muscular Dystrophy (DMD)
Status
completed
Trials
1