Wednesday, July 8, 2026

pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT

Sarepta Therapeutics

Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT · NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Clinical program

delandistrogene moxeparvovec

Phase 3 · gene therapy · Duchenne Muscular Dystrophy

delandistrogene moxeparvovec for Duchenne Muscular Dystrophy is a Phase 3 program (gene_therapy) at Sarepta Therapeutics with 7 ClinicalTrials.gov record(s).

← All Sarepta Therapeutics projects Phase 3 gene therapy active

Internal code SRP-9001-303

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Sarepta Therapeutics
Phase
Phase 3
Modality
gene_therapy
Indication
Duchenne Muscular Dystrophy
Status
active
Trials
7