Friday, July 10, 2026

pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT

Sarepta Therapeutics

Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT · NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Clinical program

SRP-9003-301

Phase 3 · small molecule · Limb-girdle muscular dystrophy, type 2E/R4 (LGMD2E/R4) or β-sarcoglycanopathy

SRP-9003-301 for Limb-girdle muscular dystrophy, type 2E/R4 (LGMD2E/R4) or β-sarcoglycanopathy is a Phase 3 program (small_molecule) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).

← All Sarepta Therapeutics projects Phase 3 small molecule active

Internal code SRP-9003-301

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Sarepta Therapeutics
Phase
Phase 3
Modality
small_molecule
Indication
Limb-girdle muscular dystrophy, type 2E/R4 (LGMD2E/R4) or β-sarcoglycanopathy
Status
active
Trials
1