🇺🇸 FDA
Pipeline program

SRP-9003

SRP-9003-101

Phase 2 gene_therapy terminated

Quick answer

SRP-9003 for Limb-Girdle Muscular Dystrophy, Type 2E is a Phase 2 program (gene_therapy) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).

Program details

Company
Sarepta Therapeutics
Indication
Limb-Girdle Muscular Dystrophy, Type 2E
Phase
Phase 2
Modality
gene_therapy
Status
terminated

Clinical trials