🇺🇸 FDA
Pipeline program

delandistrogene moxeparvovec

SRP-9001-103

Phase 2 gene_therapy active

Quick answer

delandistrogene moxeparvovec for Muscular Dystrophy, Duchenne is a Phase 2 program (gene_therapy) at Sarepta Therapeutics with 2 ClinicalTrials.gov record(s).

Program details

Company
Sarepta Therapeutics
Indication
Muscular Dystrophy, Duchenne
Phase
Phase 2
Modality
gene_therapy
Status
active

Clinical trials