Thursday, July 9, 2026

pharma · Cystic Fibrosis · Multiple Sclerosis · RARE

Ultragenyx UK

UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Bo

Newcastle upon tyne, NE128RL, GB, NOVATO, CA HQ
2024 Founded
2 Employees
Public company Type
RARE · NYSE Ticker
Company details
Status
Public
HQ
Newcastle upon tyne, NE128RL, GB, NOVATO, CA
Founded
2024
Employees
2
Programs
201
Drugs
168
Patents
23

Quick answer

UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Body Myopathy, Systemic Lupus Erythematosus. NovaPharmaNews links 201 clinical program(s), 4 drug profile(s), and 23 patent record(s) to this entity from public FDA, EMA, ClinicalTrials.gov, and USPTO sources. Pipeline phase mix: phase 2 (93), phase 3 (51), phase 1 (22).

Company snapshot

Ultragenyx UK maintains 201 tracked programs across Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Body Myopathy, Systemic Lupus Erythematosus, Systemic Sclerosis, Osteogenesis Imperfecta, Rett Syndrome, Tourette Syndrome, GNE Myopathy, Hemophilia B, Pain. Momentum score: 20/100 (30-day delta: n/a). Public registry data covers pipeline phase, clinical trials, patents,

  • 4 approved product(s) across US/EU regulatory metadata.
  • 201 active pipeline program(s) linked via ClinicalTrials.gov.
  • 23 US patent(s) indexed to this assignee profile.

Public regulatory, clinical, patent, and corporate records for Ultragenyx UK. Not investment advice.

Lead pipeline drugs

Active clinical programs

Momentum

Proprietary activity score for Ultragenyx UK.

1 active signal

20 /100 +0 vs 30 days ago

Signal breakdown

  • Clinical trials 216 30d
  • Nova articles 0 30d
  • Patents filed 0 30d
  • FDA actions 0 30d
  • SEC filings 0 30d
  • Conference presentations 0 90d
  • Pipeline advances 0 30d

Competitor landscape

Therapeutic-area overlap peers from registry and pipeline signals.

Recent activity

Latest pipeline, patent, and corporate events for Ultragenyx UK.

  1. Clinical update

    2015-1949 — Phase 3

  2. Clinical update

    AS/BW/ENE-21/0003 — Phase 1

  3. Clinical update

    whole-cell pertussis vaccine — Phase 3

  4. Clinical update

    von Willebrand factor — Phase 1

  5. Clinical update

    UX053 — Phase 2

View all clinical trial activity →

Quick answers

Common questions about this sponsor — for analysts and search.

  • What is Ultragenyx UK?

    UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Body Myopathy, Systemic Lupus Erythematosus. NovaPharmaNews li

  • Is Ultragenyx UK publicly traded?

    Yes. Ultragenyx UK is listed with ticker RARE on NYSE per SEC EDGAR records linked on this profile.

  • What drugs does Ultragenyx UK develop or market?

    We link 168 drug profile(s) where Ultragenyx UK is an originator or marketer in FDA or regional approval metadata. See the drug portfolio table on https://novapharmanews.com/companies/ultragenyx-pharmaceutical#company-drugs.

  • What are the latest developments for Ultragenyx UK?

    In the last 12 months our linked public records show 201 trial program update(s) and 2 US patent grant(s) tied to this profile.

  • What therapeutic areas does Ultragenyx UK focus on?

    Ultragenyx UK focuses on Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia based on our analysis of their pipeline programs and drug development activities.

Therapeutic focus

Therapeutic area distribution

Pipeline concentration by therapeutic area from linked clinical programs.

Programs by therapeutic area

Others
229
Infectious Disease
11
Cardiology
7
Neurology
6
Immunology
5
Oncology
1
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