Sarepta
Sarepta Therapeutics
Quick answer
Sarepta is a pharma company (SRPT) headquartered in CAMBRIDGE, MA, USA with 24 tracked pipeline programs.
Pipeline (24)
Casimersen
Duchenne Muscular Dystrophy
1 trials projectEteplirsen
Muscular Dystrophy, Duchenne
2 trials projectSRP-4045
Duchenne Muscular Dystrophy
2 trials projectSRP-9003
Limb-girdle Muscular Dystrophy
2 trials projectSRP-9005
Muscular Dystrophies, Limb-Girdle
1 trials projectdelandistrogene moxeparvovec
Duchenne Muscular Dystrophy
7 trials projecteteplirsen
Duchenne Muscular Dystrophy (DMD)
2 trials projectAVI-4065 Injection
Hepatitis C
1 trials projectAVI-4658 (Eteplirsen)
Duchenne Muscular Dystrophy (DMD)
1 trials projectAVI-4658 (Eteplirsen)
Duchenne Muscular Dystrophy
1 trials projectAVI-4658 (PMO)
Duchenne Muscular Dystrophy
1 trials projectAVI-4658 for Injection
Duchenne Muscular Dystrophy
1 trials projectAVI-5126
Cardiovascular Disease
1 trials projectAmondys 45
Duchenne Muscular Dystrophy
1 trials projectEteplirsen
Duchenne Muscular Dystrophy
2 trials projectPlacebo
Duchenne Muscular Dystrophy
1 trials projectRESTEN-MP
Coronary Artery Disease
2 trials projectSRP-5051
Muscular Dystrophy, Duchenne
2 trials projectSRP-9003
Limb-Girdle Muscular Dystrophy, Type 2E
1 trials projectSRP-9004
Limb-Girdle Muscular Dystrophy, Type 2D
1 trials projectVesleteplirsen
Duchenne Muscular Dystrophy
1 trials projectdelandistrogene moxeparvovec
Muscular Dystrophy, Duchenne
2 trials projectAVI-4020 Injection
West Nile Fever
1 trials projectAVI-4020 Injection
West Nile Virus
1 trialsDrugs (3)
Patents (8)
US 12377150
Exon skipping oligomer conjugates for muscular dystrophy
patentUS 12370261
Chimeric peptides for antisense delivery
patentUS 12286630
Treatment methods for muscular dystrophy
patentUS 12239715
Peptide oligonucleotide conjugates
patentUS 12168059
Trimeric peptides for antisense delivery
patentUS 12138312
Cell-penetrating peptides for antisense delivery
patentUS 12139709
Antisense oligomers and methods of using the same for treating diseases associat
patentUS 12121532
Modified antisense oligomers for exon inclusion in spinal muscular atrophy