🇺🇸 FDA
Company

Sarepta

Sarepta Therapeutics

SRPT pharma USA

Quick answer

Sarepta is a pharma company (SRPT) headquartered in CAMBRIDGE, MA, USA with 24 tracked pipeline programs.

Pipeline (24)

project

Casimersen

Duchenne Muscular Dystrophy

Phase 3 · small_molecule · terminated

1 trials
project

Eteplirsen

Muscular Dystrophy, Duchenne

Phase 3 · small_molecule · active

2 trials
project

SRP-4045

Duchenne Muscular Dystrophy

Phase 3 · small_molecule · completed

2 trials
project

SRP-9003

Limb-girdle Muscular Dystrophy

Phase 3 · mab · active

2 trials
project

SRP-9005

Muscular Dystrophies, Limb-Girdle

Phase 3 · mab · terminated

1 trials
project

delandistrogene moxeparvovec

Duchenne Muscular Dystrophy

Phase 3 · gene_therapy · active

7 trials
project

eteplirsen

Duchenne Muscular Dystrophy (DMD)

Phase 3 · small_molecule · completed

2 trials
project

AVI-4065 Injection

Hepatitis C

Phase 2 · small_molecule · terminated

1 trials
project

AVI-4658 (Eteplirsen)

Duchenne Muscular Dystrophy (DMD)

Phase 2 · small_molecule · completed

1 trials
project

AVI-4658 (Eteplirsen)

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · completed

1 trials
project

AVI-4658 (PMO)

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · completed

1 trials
project

AVI-4658 for Injection

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · completed

1 trials
project

AVI-5126

Cardiovascular Disease

Phase 2 · small_molecule · terminated

1 trials
project

Amondys 45

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · completed

1 trials
project

Eteplirsen

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · terminated

2 trials
project

Placebo

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · completed

1 trials
project

RESTEN-MP

Coronary Artery Disease

Phase 2 · small_molecule · completed

2 trials
project

SRP-5051

Muscular Dystrophy, Duchenne

Phase 2 · small_molecule · terminated

2 trials
project

SRP-9003

Limb-Girdle Muscular Dystrophy, Type 2E

Phase 2 · gene_therapy · terminated

1 trials
project

SRP-9004

Limb-Girdle Muscular Dystrophy, Type 2D

Phase 2 · gene_therapy · completed

1 trials
project

Vesleteplirsen

Duchenne Muscular Dystrophy

Phase 2 · small_molecule · terminated

1 trials
project

delandistrogene moxeparvovec

Muscular Dystrophy, Duchenne

Phase 2 · gene_therapy · active

2 trials
project

AVI-4020 Injection

West Nile Fever

Phase 1 · small_molecule · terminated

1 trials
project

AVI-4020 Injection

West Nile Virus

Phase 1 · small_molecule · completed

1 trials

Drugs (3)

Patents (8)