🇺🇸 FDA
Pipeline program

Eteplirsen

4658-204

Phase 3 small_molecule active

Quick answer

Eteplirsen for Muscular Dystrophy, Duchenne is a Phase 3 program (small_molecule) at Sarepta Therapeutics with 2 ClinicalTrials.gov record(s).

Program details

Company
Sarepta Therapeutics
Indication
Muscular Dystrophy, Duchenne
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials