rAAVrh74.MHCK7.DYSF.DV
IRB15-00669
Phase 1 small_molecule completed
Quick answer
rAAVrh74.MHCK7.DYSF.DV for Dysferlinopathy is a Phase 1 program (small_molecule) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Sarepta Therapeutics
- Indication
- Dysferlinopathy
- Phase
- Phase 1
- Modality
- small_molecule
- Status
- completed