Wednesday, July 8, 2026

pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT

Sarepta Therapeutics

Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT · NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Clinical program

Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53]

Approved · small molecule · Duchenne Muscular Dystrophy

Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53] for Duchenne Muscular Dystrophy is a Approved program (small_molecule) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).

← All Sarepta Therapeutics projects Approved small molecule terminated

Internal code 19-06-001

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Sarepta Therapeutics
Phase
Approved
Modality
small_molecule
Indication
Duchenne Muscular Dystrophy
Status
terminated
Trials
1