Intelligence Β· Clinical Pipeline

Ultragenyx UK Pipeline

All ClinicalTrials.gov programs at Ultragenyx UK β€” phase, modality, and trial IDs.

Programs
22

Quick answer

Ultragenyx UK has 22 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

  1. ANAWIDOW [antivenin latrodectus (black widow) equine immune F(ab)2] lyophilized powder for solution 10 mL

    Ultragenyx UK Limited

    Latrodectism

    phase 1 small molecule completed

    1 trial
  2. Acetazolamide

    Ultragenyx UK Limited

    Andersen-Tawil Syndrome

    phase 1 small molecule terminated

    1 trial
  3. Ad5-CB-CFTR

    Ultragenyx UK Limited

    Cystic Fibrosis

    phase 1 gene therapy completed

    1 trial
  4. Burosumab

    Ultragenyx UK Limited

    Cutaneous Skeletal Hypophosphatemia Syndrome (CSHS)

    phase 1 small molecule active

    1 trial
  5. CRD-TMH-001

    Ultragenyx UK Limited

    Duchenne Muscular Dystrophy

    phase 1 small molecule active

    1 trial
  6. H5.001CBCFTR

    Ultragenyx UK Limited

    Cystic Fibrosis

    phase 1 gene therapy completed

    1 trial
  7. ManNAc

    Ultragenyx UK Limited

    Hereditary Inclusion Body Myopathy (HIBM)

    phase 1 small molecule completed

    1 trial
  8. N-acetylcysteine

    Ultragenyx UK Limited

    Parkinson's Disease

    phase 1 small molecule completed

    1 trial
  9. Sargramostim

    Ultragenyx UK Limited

    Autoimmune Pulmonary Alveolar Proteinosis

    phase 1 small molecule completed

    1 trial
  10. Sialic Acid Extended Release (SA-ER) Tablets

    Ultragenyx UK Limited

    Hereditary Inclusion Body Myopathy (HIBM)

    phase 1 small molecule completed

    1 trial
  11. Triheptanoin

    Ultragenyx UK Limited

    Pyruvate Dehydrogenase Complex Deficiency

    phase 1 small molecule active

    1 trial
  12. Triheptanoin

    Ultragenyx UK Limited

    Glycogen Storage Disease Type I

    phase 1 small molecule completed

    1 trial
  13. amifostine

    Ultragenyx UK Limited

    Fanconi's Anemia

    phase 1 small molecule active

    1 trial
  14. anti-thymocyte globulin

    Ultragenyx UK Limited

    Systemic Lupus Erythematosus

    phase 1 small molecule active

    1 trial
  15. anti-thymocyte globulin

    Ultragenyx UK Limited

    Multiple Sclerosis

    phase 1 small molecule completed

    1 trial
  16. colchicine

    Ultragenyx UK Limited

    Cirrhosis

    phase 1 small molecule active

    1 trial
  17. cyclophosphamide

    Ultragenyx UK Limited

    Multiple Sclerosis

    phase 1 small molecule completed

    1 trial
  18. filgrastim

    Ultragenyx UK Limited

    Fanconi's Anemia

    phase 1 small molecule active

    1 trial
  19. gene therapy

    Ultragenyx UK Limited

    Familial Hypercholesterolemia

    phase 1 other completed

    1 trial
  20. monoclonal antibody M-T412

    Ultragenyx UK Limited

    Multiple Sclerosis

    phase 1 small molecule completed

    1 trial
  21. recombinant adenovirus containing the ornithine transcarbamylase gene

    Ultragenyx UK Limited

    Ornithine Transcarbamylase Deficiency Disease

    phase 1 gene therapy terminated

    1 trial
  22. von Willebrand factor

    Ultragenyx UK Limited

    Von Willebrand's Disease

    phase 1 small molecule completed

    1 trial

Frequently asked questions

How many pipeline programs does Ultragenyx UK have?

22 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.

Data attribution: Data sources Β· All pipeline programs