🇺🇸 FDA
Pipeline program

Acetazolamide

RDCRN 5305

Phase 1 small_molecule terminated

Quick answer

Acetazolamide for Andersen-Tawil Syndrome is a Phase 1 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Andersen-Tawil Syndrome
Phase
Phase 1
Modality
small_molecule
Status
terminated

Clinical trials