🇺🇸 FDA
Pipeline program

Sialic Acid Extended Release (SA-ER) Tablets

UX001-CL101

Phase 1 small_molecule completed

Quick answer

Sialic Acid Extended Release (SA-ER) Tablets for Hereditary Inclusion Body Myopathy (HIBM) is a Phase 1 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Hereditary Inclusion Body Myopathy (HIBM)
Phase
Phase 1
Modality
small_molecule
Status
completed

Clinical trials