H5.001CBCFTR
199/11715
Phase 1 gene_therapy completed
Quick answer
H5.001CBCFTR for Cystic Fibrosis is a Phase 1 program (gene_therapy) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Ultragenyx Pharmaceutical
- Indication
- Cystic Fibrosis
- Phase
- Phase 1
- Modality
- gene_therapy
- Status
- completed