🇺🇸 FDA

Intelligence · Clinical Pipeline

Ultragenyx UK Pipeline

All ClinicalTrials.gov programs at Ultragenyx UK — phase, modality, and trial IDs.

Programs
93

Quick answer

Ultragenyx UK has 93 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

  1. -aminosalicylic acid

    Ultragenyx UK Limited

    Ulcerative Colitis

    phase 2 small molecule completed

    1 trial

  2. AVTX-801

    Ultragenyx UK Limited

    SLC35A2-CDG - Solute Carrier Family 35 Member A2 Congenital Disorder of Glycosylation

    phase 2 small molecule active

    1 trial

  3. Abatacept

    Ultragenyx UK Limited

    Takayasu's Arteritis

    phase 2 small molecule completed

    1 trial

  4. Abatacept

    Ultragenyx UK Limited

    Wegener's Granulomatosis

    phase 2 small molecule completed

    1 trial

  5. Aceneuramic Acid Extended-Release

    Ultragenyx UK Limited

    Hereditary Inclusion Body Myopathy

    phase 2 small molecule terminated

    1 trial

  6. Antithymocyte globulin (ATG)

    Ultragenyx UK Limited

    Myelodysplastic Syndrome

    phase 2 small molecule active

    1 trial

  7. BPS804

    Ultragenyx UK Limited

    Osteogenesis Imperfecta

    phase 2 small molecule completed

    1 trial

  8. Cisplatin

    Ultragenyx UK Limited

    Squamous Cell Carcinoma of the Anus

    phase 2 small molecule active

    1 trial

  9. Colchicine

    Ultragenyx UK Limited

    Primary Cutaneous Vasculitis

    phase 2 small molecule active

    1 trial

  10. DTX101

    Ultragenyx UK Limited

    Hemophilia B

    phase 2 gene therapy terminated

    1 trial

  11. DTX401

    Ultragenyx UK Limited

    GSD1

    phase 2 gene therapy completed

    1 trial

  12. Exercise

    Ultragenyx UK Limited

    Spinal Cord Injury

    phase 2 other completed

    1 trial

  13. GLUT1 DS

    Ultragenyx UK Limited

    Glut1 Deficiency Syndrome

    phase 2 small molecule completed

    1 trial

  14. Hydroxyproline and Leucine

    Ultragenyx UK Limited

    Hyperoxaluria

    phase 2 small molecule completed

    1 trial

  15. Losartan Potassium

    Ultragenyx UK Limited

    Eosinophilic Esophagitis

    phase 2 small molecule completed

    1 trial

  16. Melphalan

    Ultragenyx UK Limited

    Amyloidosis

    phase 2 small molecule completed

    1 trial

  17. N-acetylcysteine

    Ultragenyx UK Limited

    Gaucher Disease Type 1

    phase 2 small molecule completed

    1 trial

  18. NTBC

    Ultragenyx UK Limited

    Tyrosinemia, Type I

    phase 2 small molecule completed

    1 trial

  19. POST Triheptanoin

    Ultragenyx UK Limited

    Frontal Lobe Hypometabolism

    phase 2 small molecule completed

    1 trial

  20. RAD001

    Ultragenyx UK Limited

    PTEN Gene Mutation

    phase 2 small molecule completed

    1 trial

  21. SA-ER 500 mg

    Ultragenyx UK Limited

    GNE Myopathy

    phase 2 small molecule completed

    1 trial

  22. SDZ MSL-109

    Ultragenyx UK Limited

    Cytomegalovirus Infections

    phase 2 small molecule completed

    1 trial

  23. Sialic Acid Extended Release (SA-ER)

    Ultragenyx UK Limited

    GNE Myopathy

    phase 2 small molecule completed

    1 trial

  24. Sirolimus

    Ultragenyx UK Limited

    Anemia, Aplastic

    phase 2 small molecule active

    1 trial

  25. Sirolimus 0.5 mg

    Ultragenyx UK Limited

    Beta-Thalassemia

    phase 2 small molecule active

    2 trials

  26. Sodium Benzoate

    Ultragenyx UK Limited

    Amino Acid Metabolism, Inborn Errors

    phase 2 small molecule completed

    1 trial

  27. Sodium Phenylbutyrate

    Ultragenyx UK Limited

    Argininosuccinic Aciduria

    phase 2 small molecule completed

    1 trial

  28. Surgery

    Ultragenyx UK Limited

    Spastic Diplegia

    phase 2 other active

    1 trial

  29. Tiratricol

    Ultragenyx UK Limited

    Allan-Herndon-Dudley Syndrome

    phase 2 small molecule active

    1 trial

  30. Tridecanoic Acid

    Ultragenyx UK Limited

    Rett Syndrome

    phase 2 small molecule active

    1 trial

  31. Triheptanoin

    Ultragenyx UK Limited

    Glucose Transporter Type-1 Deficiency Syndrome (Glut1 DS)

    phase 2 small molecule completed

    1 trial

  32. Triheptanoin

    Ultragenyx UK Limited

    Adult Polyglucosan Body Disease

    phase 2 small molecule completed

    1 trial

  33. Triheptanoin

    Ultragenyx UK Limited

    ALS

    phase 2 small molecule completed

    1 trial

  34. Triheptanoin

    Ultragenyx UK Limited

    Glucose Transporter Type 1 Deficiency Syndrome

    phase 2 small molecule active

    1 trial

  35. Triheptanoin

    Ultragenyx UK Limited

    Glycogen Storage Disease Type V

    phase 2 small molecule completed

    1 trial

  36. Triheptanoin

    Ultragenyx UK Limited

    Medium-chain Acyl-CoA Dehydrogenase Deficiency

    phase 2 small molecule active

    2 trials

  37. Triheptanoin

    Ultragenyx UK Limited

    Tarui Disease

    phase 2 small molecule completed

    1 trial

  38. Triheptanoin oil

    Ultragenyx UK Limited

    Huntington Disease

    phase 2 small molecule completed

    1 trial

  39. UX003

    Ultragenyx UK Limited

    Mucopolysaccharidosis Type 7

    phase 2 small molecule completed

    1 trial

  40. UX007

    Ultragenyx UK Limited

    Glucose Transporter Type 1 Deficiency Syndrome

    phase 2 small molecule terminated

    1 trial

  41. UX007

    Ultragenyx UK Limited

    Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)

    phase 2 small molecule completed

    1 trial

  42. UX007

    Ultragenyx UK Limited

    Carnitine Palmitoyltransferase (CPT I or CPT II) Deficiency

    phase 2 small molecule completed

    1 trial

  43. UX016

    Ultragenyx UK Limited

    GNE Myopathy

    phase 2 small molecule active

    1 trial

  44. UX053

    Ultragenyx UK Limited

    Glycogen Storage Disease Type III

    phase 2 mab terminated

    1 trial

  45. UX701

    Ultragenyx UK Limited

    Wilson Disease

    phase 2 gene therapy active

    1 trial

  46. [6,6-2H2]glucose

    Ultragenyx UK Limited

    Glycogen Storage Disease Type IA

    phase 2 mab completed

    1 trial

  47. allopurinol

    Ultragenyx UK Limited

    Leishmaniasis

    phase 2 small molecule completed

    1 trial

  48. aminomidazole carboxamide riboside

    Ultragenyx UK Limited

    Lesch-Nyhan Syndrome

    phase 2 small molecule completed

    1 trial

Frequently asked questions

How many pipeline programs does Ultragenyx UK have?

93 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.

Data attribution: Data sources · All pipeline programs

Drug approvals, clinical trials, M&A, event intelligence, and company updates — weekly.

Customize topics & region
Topics
Region

No spam. Unsubscribe anytime. See our privacy policy.