Intelligence Β· Clinical Pipeline

Ultragenyx UK Pipeline

All ClinicalTrials.gov programs at Ultragenyx UK β€” phase, modality, and trial IDs.

Programs
5

Quick answer

Ultragenyx UK has 5 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

  1. Crysvita (burosumab-twza) Treatment

    Ultragenyx UK Limited

    Epidermal Nevus Syndrome

    approved small molecule completed

    1 trial
  2. Leucovorin calcium

    Ultragenyx UK Limited

    Toxoplasmosis

    approved small molecule active

    1 trial
  3. Osilodrostat (Isturisa)

    Ultragenyx UK Limited

    Mild Autonomous Cortisol Secretion (MACS)

    approved small molecule active

    1 trial
  4. epoprostenol

    Ultragenyx UK Limited

    Hypertension, Pulmonary

    approved small molecule completed

    1 trial
  5. miglustat

    Ultragenyx UK Limited

    GM1 Gangliosidoses

    approved small molecule terminated

    1 trial

Frequently asked questions

How many pipeline programs does Ultragenyx UK have?

5 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.

Data attribution: Data sources Β· All pipeline programs