recombinant adenovirus containing the ornithine transcarbamylase gene
199/12054
Phase 1 gene_therapy terminated
Quick answer
recombinant adenovirus containing the ornithine transcarbamylase gene for Ornithine Transcarbamylase Deficiency Disease is a Phase 1 program (gene_therapy) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Ultragenyx Pharmaceutical
- Indication
- Ornithine Transcarbamylase Deficiency Disease
- Phase
- Phase 1
- Modality
- gene_therapy
- Status
- terminated