🇺🇸 FDA
Pipeline program

gene therapy

199/12011

Phase 1 other completed

Quick answer

gene therapy for Familial Hypercholesterolemia is a Phase 1 program (other) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Familial Hypercholesterolemia
Phase
Phase 1
Modality
other
Status
completed

Clinical trials