pharma · Cystic Fibrosis · Multiple Sclerosis · RARE
Ultragenyx UK
Ultragenyx UK Limited
UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Bo
Company details
- Status
- Public
- HQ
- Newcastle upon tyne, NE128RL, GB, NOVATO, CA
- Founded
- 2024
- Employees
- 2
- Programs
- 201
- Drugs
- 168
- Patents
- 23
gene therapy
Phase 1 · other · Familial Hypercholesterolemia
gene therapy for Familial Hypercholesterolemia is a Phase 1 program (other) at Ultragenyx UK Limited with 1 ClinicalTrials.gov record(s).
Internal code 199/12011
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- Ultragenyx UK Limited
- Phase
- Phase 1
- Modality
- other
- Indication
- Familial Hypercholesterolemia
- Status
- completed
- Trials
- 1