🇺🇸 FDA
Pipeline program

Ad5-CB-CFTR

199/11829

Phase 1 gene_therapy completed

Quick answer

Ad5-CB-CFTR for Cystic Fibrosis is a Phase 1 program (gene_therapy) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Cystic Fibrosis
Phase
Phase 1
Modality
gene_therapy
Status
completed

Clinical trials