🇺🇸 FDA
Pipeline program

Triheptanoin

STUDY23050042

Phase 1 small_molecule active

Quick answer

Triheptanoin for Pyruvate Dehydrogenase Complex Deficiency is a Phase 1 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Pyruvate Dehydrogenase Complex Deficiency
Phase
Phase 1
Modality
small_molecule
Status
active

Clinical trials