🇺🇸 FDA
Pipeline program

Ataluren

PTC124-GD-028e- ANI

Phase 2 small_molecule terminated

Quick answer

Ataluren for Aniridia is a Phase 2 program (small_molecule) at PTC THERAPEUTICS, INC. with 2 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
Aniridia
Phase
Phase 2
Modality
small_molecule
Status
terminated

Clinical trials