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Drug profile · INN

onasemnogene abeparvovec

onasemnogene abeparvovec (ZOLGENSMA) is a survival motor neuron protein exogenous gene. Associated with Novartis Pharmaceuticals.

EMA: approved TGA: approved Musculo-skeletal system (M09) M09AX09
Patents linked 0
Pipeline programs 2
News articles 2
Drug details — onasemnogene abeparvovec

Quick answer

onasemnogene abeparvovec (ZOLGENSMA) is a survival motor neuron protein exogenous gene. Associated with Novartis Pharmaceuticals.

Key facts

INN onasemnogene abeparvovec
Brand ZOLGENSMA
Mechanism Survival motor neuron protein exogenous gene
Target Survival motor neuron protein
Therapeutic class Musculo-skeletal system (M09)
ATC code M09AX09

Mechanism of action

Survival motor neuron protein exogenous gene

Primary target: Survival motor neuron protein

Approval history

Authority Status Date
EMA approved
TGA approved

Recent coverage

Pipeline programs

  1. COAV101A12308 Phase 3 · Novartis India · Spinal Muscular Atrophy
  2. Zolgensma 2 × 10^13 vector genomes/mL solution for infusion Phase 3 · Novartis India · Spinal Muscular Atrophy

Related & competitor drugs

  1. allopurinol Musculo-skeletal system (M04)
  2. colchicine Musculo-skeletal system (M04)
  3. denosumab Musculo-skeletal system (M05)
  4. eteplirsen Musculo-skeletal system (M09)
  5. febuxostat Musculo-skeletal system (M04)
  6. ibandronic acid Musculo-skeletal system (M05)

Frequently asked questions

What is onasemnogene abeparvovec?

onasemnogene abeparvovec (ZOLGENSMA) is a survival motor neuron protein exogenous gene. Associated with Novartis Pharmaceuticals.

What is the brand name for onasemnogene abeparvovec?

ZOLGENSMA is a marketed brand name for onasemnogene abeparvovec. Check FDA Drugs@FDA for the current US label holder and prescribing information.