IONIS
IONIS PHARMACEUTICALS INC
Quick answer
IONIS is a pharma company (IONS) headquartered in CARLSBAD, CA, USA with 24 tracked pipeline programs.
Pipeline (24)
Alicaforsen
Crohn's Disease
2 trials projectDonidalorsen
Hereditary Angioedema (HAE)
1 trials projectDonidalorsen
Hereditary Angioedema
4 trials projectEplontersen
Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)
2 trials projectEplontersen
Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
1 trials projectION363
Amyotrophic Lateral Sclerosis
1 trials projectION582
Angelman Syndrome
2 trials projectISIS 3521
Lung Cancer
1 trials projectInotersen
Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
1 trials projectInotersen
FAP
2 trials projectMipomersen
Hypercholesterolemia
1 trials projectMipomersen sodium
Hypercholesterolemia
1 trials projectOlezarsen
Severe Hypertriglyceridemia
3 trials projectOlezarsen
Familial Chylomicronemia Syndrome
3 trials projectOlezarsen
Hypertriglyceridemia
2 trials projectTofersen
ALS Caused by Superoxide Dismutase 1 (SOD1) Mutation
1 trials projectTofersen
Amyotrophic Lateral Sclerosis
1 trials projectVolanesorsen
Hypertriglyceridemia
1 trials projectVolanesorsen
Familial Chylomicronemia Syndrome
2 trials projectmipomersen
Lipid Metabolism, Inborn Errors
2 trials projectmipomersen sodium
Heterozygous Familial Hypercholesterolemia
1 trials projectmipomersen sodium
Lipid Metabolism, Inborn Errors
2 trials projectvolanesorsen
Familial Partial Lipodystrophy
1 trials projectzilganersen
Alexander Disease
1 trialsDrugs (2)
Patents (8)
US 12409188
Modulators of HSD17B13 expression
patentUS 12410430
Modulating apolipoprotein (A) expression
patentUS 12410225
Modulation of dendritic cell lineages
patentUS 12364753
CD8 binding agents
patentUS 12350285
Compounds and methods for reducing ATXN3 expression
patentUS 12351614
CLEC9A-based chimeric protein complexes
patentUS 12351633
PD-1 and PD-L1 binding agents
patentUS 12343357
Compositions and methods for modulating MECP2 expression