🇺🇸 FDA
Pipeline program

Deflazacort

PTCEMF-GD-004

Phase 3 small_molecule terminated

Quick answer

Deflazacort for Limb-Girdle Muscular Dystrophy is a Phase 3 program (small_molecule) at PTC THERAPEUTICS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
Limb-Girdle Muscular Dystrophy
Phase
Phase 3
Modality
small_molecule
Status
terminated

Clinical trials