🇺🇸 FDA
Company

PTC

PTC THERAPEUTICS, INC.

PTCT pharma USA

Quick answer

PTC is a pharma company (PTCT) headquartered in WARREN, NJ, USA with 24 tracked pipeline programs.

Pipeline (24)

project

Ataluren

Duchenne Muscular Dystrophy

Phase 3 · small_molecule · terminated

9 trials project

Ataluren

Muscular Dystrophy, Duchenne

Phase 3 · small_molecule · terminated

3 trials project

Ataluren

Cystic Fibrosis

Phase 3 · small_molecule · completed

6 trials project

Ataluren (PTC124®)

Cystic Fibrosis

Phase 3 · small_molecule · completed

1 trials project

Deflazacort

Duchenne Muscular Dystrophy

Phase 3 · small_molecule · completed

3 trials project

Deflazacort

Limb-Girdle Muscular Dystrophy

Phase 3 · small_molecule · terminated

1 trials project

PTC299

Pneumonia

Phase 3 · small_molecule · terminated

1 trials project

PTC923

Phenylketonuria

Phase 3 · small_molecule · active

2 trials project

Sepiapterin

Phenylketonuria

Phase 3 · small_molecule · active

1 trials project

Unesbulin

Leiomyosarcoma

Phase 3 · small_molecule · terminated

2 trials project

Vatiquinone

Friedreich Ataxia

Phase 3 · small_molecule · active

3 trials project

Vatiquinone

Mitochondrial Diseases

Phase 3 · small_molecule · terminated

1 trials project

Vatiquinone

Inherited Mitochondrial Disease

Phase 3 · small_molecule · completed

1 trials project

AAV2-hAADC

Aromatic Amino Acid Decarboxylase Deficiency

Phase 2 · small_molecule · completed

1 trials project

Ataluren

Amino Acid Metabolism, Inborn Errors

Phase 2 · small_molecule · terminated

1 trials project

Ataluren

Nonsene Mutation Duchenne Muscular Dystrophy

Phase 2 · small_molecule · completed

1 trials project

Ataluren

Hemophilia A

Phase 2 · small_molecule · terminated

1 trials project

Ataluren

Aniridia

Phase 2 · small_molecule · terminated

2 trials project

Ataluren + Pembrolizumab

Colorectal Cancer

Phase 2 · small_molecule · active

1 trials project

CNSA-001

Gastroparesis

Phase 2 · small_molecule · completed

1 trials project

EPI-589

Amyotrophic Lateral Sclerosis

Phase 2 · small_molecule · completed

1 trials project

EPI-743

Leigh Syndrome

Phase 2 · small_molecule · completed

1 trials project

Eladocagene Exuparvovec

AADC Deficiency

Phase 2 · gene_therapy · active

1 trials project

PTC124

Cystic Fibrosis

Phase 2 · small_molecule · completed

2 trials

Drugs (1)

drug

sepiapterin

SEPHIENCE

Patents (8)

patent

US 12398140

Substituted pyrrolo [2,3-d]pyrimidines for treating familial dysautonomia

Expires Mon Aug 21 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12384797

Thioeno[3,2-b] pyridin-7-amine compounds for treating familial dysautonomia

Expires Mon Aug 07 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12384789

Compounds for treating Huntington's disease

Expires Mon Aug 07 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12281083

2-substituted amino-naphth (1,2-d) imidazol-5-one compounds of pharmaceutically

Expires Mon Apr 17 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12139499

Heteroaryl compounds for treating Huntington's disease

Expires Mon Nov 07 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12103926

Compounds for treating huntington's disease

Expires Mon Sep 26 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12023335

Method for treating pancreatic cancer

Expires Mon Jun 27 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 11938101

Polymorphic forms of (R)-2-hydroxy-2-methyl-4-(2,4,5-trimethyl-3,6-dioxocyclohex

Expires Mon Mar 21 2044 00:00:00 GMT+0000 (Coordinated Universal Time)