🇺🇸 FDA
Pipeline program

Ataluren

PTC124-GD-005-CF

Phase 3 small_molecule completed

Quick answer

Ataluren for Cystic Fibrosis is a Phase 3 program (small_molecule) at PTC THERAPEUTICS, INC. with 6 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
Cystic Fibrosis
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials