Drug profile · INN
golodirsen
VYONDYS 53
golodirsen (VYONDYS 53) is a dystrophin pre-mrna positive modulator. Associated with Sarepta Therapeutics. Route of administration: intravenous. Current US regulatory status: approved.
Drug details — golodirsen
- US status
- approved
- Class
- —
- Route
- INTRAVENOUS
- Patents
- 20
- Programs
- 2
- Data quality
- 0.89
Quick answer
golodirsen (VYONDYS 53) is a dystrophin pre-mrna positive modulator. Associated with Sarepta Therapeutics. Route of administration: intravenous. Current US regulatory status: approved.
Key facts
Mechanism of action
Dystrophin pre-mRNA positive modulator
Primary target: Dystrophin pre-mRNA
Approval history
| Authority | Status | Date |
|---|---|---|
| FDA | approved | — |
Pipeline programs
Related & competitor drugs
Related patents
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Frequently asked questions
What is golodirsen?
golodirsen (VYONDYS 53) is a dystrophin pre-mrna positive modulator. Associated with Sarepta Therapeutics. Route of administration: intravenous. Current US regulatory status: approved.
What is the brand name for golodirsen?
VYONDYS 53 is a marketed brand name for golodirsen. Check FDA Drugs@FDA for the current US label holder and prescribing information.
What is the US approval status of golodirsen?
golodirsen has approved status in the United States according to our Drugs@FDA-derived records. Verify on the official FDA label before clinical or commercial decisions.