Intelligence · Clinical Pipeline
PTC THERAPEUTICS Pipeline
All ClinicalTrials.gov programs at PTC THERAPEUTICS — phase, modality, and trial IDs.
- Programs
- 23
Quick answer
PTC THERAPEUTICS has 23 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.
-
AAV2-hAADC
PTC THERAPEUTICS, INC.
Aromatic Amino Acid Decarboxylase Deficiency
1 trial -
Ataluren
PTC THERAPEUTICS, INC.
Amino Acid Metabolism, Inborn Errors
1 trial -
Ataluren
PTC THERAPEUTICS, INC.
Aniridia
2 trials -
Ataluren
PTC THERAPEUTICS, INC.
Hemophilia A
1 trial -
Ataluren
PTC THERAPEUTICS, INC.
Nonsene Mutation Duchenne Muscular Dystrophy
1 trial -
Ataluren + Pembrolizumab
PTC THERAPEUTICS, INC.
Colorectal Cancer
1 trial -
CNSA-001
PTC THERAPEUTICS, INC.
Gastroparesis
1 trial -
EPI-589
PTC THERAPEUTICS, INC.
Amyotrophic Lateral Sclerosis
1 trial -
EPI-743
PTC THERAPEUTICS, INC.
Leigh Syndrome
1 trial -
Eladocagene Exuparvovec
PTC THERAPEUTICS, INC.
AADC Deficiency
1 trial -
PTC124
PTC THERAPEUTICS, INC.
Duchenne Muscular Dystrophy
1 trial -
PTC124
PTC THERAPEUTICS, INC.
Cystic Fibrosis
2 trials -
PTC299
PTC THERAPEUTICS, INC.
Neurofibromatosis 2
1 trial -
PTC518
PTC THERAPEUTICS, INC.
Huntington Disease
1 trial -
PTC857
PTC THERAPEUTICS, INC.
Amyotrophic Lateral Sclerosis
1 trial -
PTC857, Placebo to match PTC857 60 mg/mL oral solution, Utreloxastat 62.5
PTC THERAPEUTICS, INC.
Amyotrophic Lateral Sclerosis
1 trial -
PTC923
PTC THERAPEUTICS, INC.
BH4 Deficiency
1 trial -
Placebo
PTC THERAPEUTICS, INC.
Friedreich's Ataxia
1 trial -
Placebo
PTC THERAPEUTICS, INC.
Leigh Syndrome
1 trial -
Placebo to match 5-mg PTC518 tablets, Placebo to match 20-mg PTC518 tablets, PTC518, PTC518
PTC THERAPEUTICS, INC.
Huntington’s Disease
1 trial -
VEGF inhibitor PTC299
PTC THERAPEUTICS, INC.
Kaposi's Sarcoma
1 trial -
ataluren
PTC THERAPEUTICS, INC.
Epilepsy
1 trial -
gene therapy
PTC THERAPEUTICS, INC.
Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
1 trial
Frequently asked questions
How many pipeline programs does PTC THERAPEUTICS have?
23 published programs are linked to this sponsor in our ClinicalTrials.gov index.
Is this the complete company pipeline?
This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.
Data attribution: Data sources · All pipeline programs