🇺🇸 FDA
Pipeline program

PTC923

PBD-001

Phase 2 small_molecule completed

Quick answer

PTC923 for BH4 Deficiency is a Phase 2 program (small_molecule) at PTC THERAPEUTICS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
BH4 Deficiency
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials