Ataluren
PTC124-GD-012-MMA
Phase 2 small_molecule terminated
Quick answer
Ataluren for Amino Acid Metabolism, Inborn Errors is a Phase 2 program (small_molecule) at PTC THERAPEUTICS, INC. with 1 ClinicalTrials.gov record(s).
Program details
- Company
- PTC THERAPEUTICS, INC.
- Indication
- Amino Acid Metabolism, Inborn Errors
- Phase
- Phase 2
- Modality
- small_molecule
- Status
- terminated