🇺🇸 FDA
Pipeline program

Ataluren

PTC124-GD-048-DMD

Phase 2 small_molecule completed

Quick answer

Ataluren for Nonsene Mutation Duchenne Muscular Dystrophy is a Phase 2 program (small_molecule) at PTC THERAPEUTICS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
Nonsene Mutation Duchenne Muscular Dystrophy
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials