🇺🇸 FDA
Pipeline program

PTC124

PTC124-GD-005e-CF

Phase 2 small_molecule completed

Quick answer

PTC124 for Cystic Fibrosis is a Phase 2 program (small_molecule) at PTC THERAPEUTICS, INC. with 2 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
Cystic Fibrosis
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials