Tuesday, July 21, 2026

pharma · TTR-mediated Amyloidosis · Hypertension · ALNY

Alnylam Netherlands

Alnylam Netherlands drug portfolio — 24 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Cambridge, USA HQ
2002 Founded
2,826 Employees
Public company Type
ALNY · NYSE Ticker
Company details
Status
Public
HQ
Cambridge, USA
Founded
2002
Employees
2,826
Programs
1
Drugs
24
Patents
34
Intelligence · Drug Pipeline

Alnylam Netherlands pipeline

Portfolio lens on 24 drugs and development assets — regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Alnylam Netherlands drug portfolio — 24 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

24 compounds
  1. abacavir

    Antiinfectives for systemic use (J05)

    US regulatory status: approved.

  2. US regulatory status: approved. Molecular target: Fatty-acid amide hydrolase 1.

    Target
    Fatty-acid amide hydrolase 1
    Mechanism
    Cyclooxygenase inhibitor
  3. US regulatory status: approved. Molecular target: DNA polymerase catalytic subunit.

    Target
    DNA polymerase catalytic subunit
    Mechanism
    Human herpesvirus 1 DNA polymerase inhibitor
  4. US regulatory status: approved.

  5. US regulatory status: approved.

  6. colchicine

    Musculo-skeletal system (M04)

    US regulatory status: approved. Molecular target: Tubulin.

    Target
    Tubulin
    Mechanism
    Tubulin inhibitor
  7. US regulatory status: approved. Molecular target: Estrogen receptor.

    Target
    Estrogen receptor
    Mechanism
    Estrogen receptor alpha agonist
  8. givosiran

    Alimentary tract and metabolism (A16)

    Alimentary tract and metabolism (A16) compound in Alnylam Netherlands's portfolio. Molecular target: 5-aminolevulinate synthase mRNA.

    Target
    5-aminolevulinate synthase mRNA
    Mechanism
    5-aminolevulinate synthase mRNA RNAi inhibitor
  9. US regulatory status: approved. Molecular target: 5-aminolevulinate synthase mRNA.

    Target
    5-aminolevulinate synthase mRNA
    Mechanism
    5-aminolevulinate synthase mRNA RNAi inhibitor
  10. US regulatory status: approved. Molecular target: Enoyl-[acyl-carrier-protein] reductase [NADH] FabI.

    Target
    Enoyl-[acyl-carrier-protein] reductase [NADH] FabI
    Mechanism
    Bacterial enoyl-[acyl-carrier-protein] reductase inhibitor
  11. US regulatory status: approved. Molecular target: Solute carrier family 12 member 3.

    Target
    Solute carrier family 12 member 3
    Mechanism
    Thiazide-sensitive sodium-chloride cotransporter inhibitor
  12. lumasiran

    Alimentary tract and metabolism (A16)

    Alimentary tract and metabolism (A16) compound in Alnylam Netherlands's portfolio. Mechanism: Hydroxyacid oxidase 1 mRNA RNAi inhibitor.

    Mechanism
    Hydroxyacid oxidase 1 mRNA RNAi inhibitor
  13. US regulatory status: approved. Molecular target: Hydroxyacid oxidase 1 mRNA.

    Target
    Hydroxyacid oxidase 1 mRNA
    Mechanism
    Hydroxyacid oxidase 1 mRNA RNAi inhibitor
  14. US regulatory status: approved. Molecular target: Progesterone receptor.

    Target
    Progesterone receptor
    Mechanism
    Progesterone receptor agonist
  15. patisiran

    Nervous system (N07)

    Nervous system (N07) compound in Alnylam Netherlands's portfolio. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin mRNA RNAi inhibitor
  16. US regulatory status: approved. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin mRNA RNAi inhibitor
  17. US regulatory status: approved. Molecular target: Complement C5.

    Target
    Complement C5
    Mechanism
    Complement C5 inhibitor
  18. US regulatory status: approved. Molecular target: Retinoic acid receptor.

    Target
    Retinoic acid receptor
    Mechanism
    Retinoic acid receptor agonist
  19. vutrisiran

    Nervous system (N07)

    Nervous system (N07) compound in Alnylam Netherlands's portfolio. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin mRNA rnai inhibitor
  20. US regulatory status: approved. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin mRNA rnai inhibitor