🇺🇸 FDA
Company

BIOMARIN

BIOMARIN PHARMACEUTICAL INC

BMRN pharma USA

Quick answer

BIOMARIN is a pharma company (BMRN) headquartered in NOVATO, CA, USA with 24 tracked pipeline programs.

Pipeline (24)

project

Aldurazyme

Mucopolysaccharidosis I

Phase 3 · mab · completed

1 trials project

BMN 110

Mucopolysaccharidosis IVA (Morquio A Syndrome)

Phase 3 · small_molecule · completed

1 trials project

BMN 110 - Weekly

Mucopolysaccharidosis IV A

Phase 3 · small_molecule · completed

1 trials project

BMN 110 Weekly

MPS IV A

Phase 3 · small_molecule · completed

1 trials project

BMN 111

Achondroplasia

Phase 3 · small_molecule · active

6 trials project

BMN 165

Phenylketonuria

Phase 3 · small_molecule · completed

1 trials project

BMN 333

Achondroplasia

Phase 3 · small_molecule · active

1 trials project

BMN 701

Late-onset Pompe Disease

Phase 3 · small_molecule · terminated

1 trials project

BMN165 20mg/day

Phenylketonuria (PKU)

Phase 3 · small_molecule · completed

1 trials project

Drisapersen

Muscular Dystrophies

Phase 3 · small_molecule · terminated

2 trials project

INZ-701

Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency

Phase 3 · small_molecule · active

2 trials project

Kuvan®

Autistic Disorder

Phase 3 · small_molecule · completed

1 trials project

N-acetylgalactosamine 4-sulfatase

Mucopolysaccharidosis VI

Phase 3 · small_molecule · completed

3 trials project

Pegvaliase

Phenylketonuria (PKU)

Phase 3 · small_molecule · active

2 trials project

Placebo

Mucopolysaccharidosis VI

Phase 3 · small_molecule · completed

1 trials project

Sapropterin Dihydrochloride

Phenylketonurias

Phase 3 · small_molecule · completed

3 trials project

Sapropterin dihydrochloride

Phenylketonuria

Phase 3 · small_molecule · completed

4 trials project

Vosoritide

Hypochondroplasia

Phase 3 · small_molecule · active

3 trials project

rhIDU (recombinant human-Alpha-L-Iduronidase)

Mucopolysaccharidosis I

Phase 3 · mab · completed

1 trials project

sapropterin

Behavioral Manifestations of Lesch-Nyhan Disease

Phase 3 · small_molecule · terminated

1 trials project

sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin

Phenylketonurias

Phase 3 · small_molecule · completed

1 trials project

valoctocogene roxaparvovec

Hemophilia A

Phase 3 · mab · active

5 trials project

6R BH4

Kidney Disease

Phase 2 · small_molecule · completed

1 trials project

6R-BH4

Coronary Artery Disease

Phase 2 · small_molecule · active

1 trials

Drugs (7)

drug

cerliponase alfa

BRINEURA

 drug

elosulfase alfa

VIMIZIM

 drug

galsulfase

NAGLAZYME

 drug

laronidase

ALDURAZYME

 drug

pegvaliase-pqpz

PALYNZIQ

 drug

sapropterin dihydrochloride

SAPROPTERIN DIHYDROCHLORIDE

 drug

vosoritide

VOXZOGO

Patents (8)

patent

US 12427171

Krill oil composition enriched in LPC-DHA and LPC-EPA

Expires Mon Sep 25 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12331293

Bispecific antisense oligonucleotides for dystrophin exon skipping

Expires Mon Jun 12 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12239692

Adeno-associated virus factor VIII vectors

Expires Mon Feb 27 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12233106

C-type natriuretic peptide variants to treat skeletal dysplasia in children

Expires Mon Feb 20 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12214015

Use of c-type natriuretic peptide variants to treat osteoarthritis

Expires Mon Jan 30 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12194064

Process of producing concentrated therapeutic phospholipid composition from kril

Expires Mon Jan 09 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12188058

Manufacture of active highly phosphorylated human lysosomal sulfatase enzymes an

Expires Mon Jan 02 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

 patent

US 12076333

Lysophosphatidylcholine compositions

Expires Mon Aug 29 2044 00:00:00 GMT+0000 (Coordinated Universal Time)