Friday, July 10, 2026

Drug profile · INN

pegvaliase

pegvaliase (PALYNZIQ) is a phenylalanine hydrolytic enzyme. Associated with BioMarin Pharmaceutical Australia Pty Ltd.

EMA: approved Alimentary tract and metabolism (A16) A16AB19
Patents linked 0
Pipeline programs 7
News articles 0
Drug details — pegvaliase
Class
Alimentary tract and metabolism (A16)
Route
Patents
0
Programs
7
Data quality
0.89

Quick answer

pegvaliase (PALYNZIQ) is a phenylalanine hydrolytic enzyme. Associated with BioMarin Pharmaceutical Australia Pty Ltd.

Key facts

INN pegvaliase
Brand PALYNZIQ
Mechanism Phenylalanine hydrolytic enzyme
Target Phenylalanine
Therapeutic class Alimentary tract and metabolism (A16)
ATC code A16AB19

Mechanism of action

Phenylalanine hydrolytic enzyme

Primary target: Phenylalanine

Approval history

Authority Status Date
EMA approved

Pipeline programs

  1. 165-306 Phase 3 · BioMarin Pharmaceutical Australia · Phenylketonuria (PKU)
  2. Pegvaliase Phase 3 · BioMarin Pharmaceutical Australia · Phenylketonuria (PKU)
  3. BMN 165 (rAvPAL-PEG) Phase 2 · BioMarin Pharmaceutical Australia · Phenylketonuria
  4. rAvPAL-PEG Phase 2 · BioMarin Pharmaceutical Australia · Phenylketonuria
  5. rAvPAL-PEG 0.001 mg/kg Phase 2 · BioMarin Pharmaceutical Australia · Phenylketonuria
  6. Pegvaliase Approved · BioMarin Pharmaceutical Australia · Phenylketonuria
  7. RDD to Palynziq Approved · BioMarin Pharmaceutical Australia · Phenylketonuria

Related & competitor drugs

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  2. alogliptin Alimentary tract and metabolism (A10)
  3. alogliptin benzoate Alimentary tract and metabolism (A10)
  4. aprepitant Alimentary tract and metabolism (A04)
  5. budesonide Alimentary tract and metabolism (A07)
  6. canagliflozin Alimentary tract and metabolism (A10)

Frequently asked questions

What is pegvaliase?

pegvaliase (PALYNZIQ) is a phenylalanine hydrolytic enzyme. Associated with BioMarin Pharmaceutical Australia Pty Ltd.

What is the brand name for pegvaliase?

PALYNZIQ is a marketed brand name for pegvaliase. Check FDA Drugs@FDA for the current US label holder and prescribing information.