Pegvaliase
165-304
Phase 3 small_molecule active
Quick answer
Pegvaliase for Phenylketonuria (PKU) is a Phase 3 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 2 ClinicalTrials.gov record(s).
Program details
- Company
- BIOMARIN PHARMACEUTICAL INC
- Indication
- Phenylketonuria (PKU)
- Phase
- Phase 3
- Modality
- small_molecule
- Status
- active