🇺🇸 FDA
Pipeline program

Crysvita (burosumab-twza) Treatment

IRB-300004900

Approved small_molecule completed

Quick answer

Crysvita (burosumab-twza) Treatment for Epidermal Nevus Syndrome is a Approved program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Epidermal Nevus Syndrome
Phase
Approved
Modality
small_molecule
Status
completed

Clinical trials