pharma · Cystic Fibrosis · Multiple Sclerosis · RARE
Ultragenyx UK
Ultragenyx UK Limited
UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Bo
Newcastle upon tyne, NE128RL, GB, NOVATO, CA HQ
2024 Founded
2 Employees
Public company Type
RARE · NYSE Ticker
Company details
- Status
- Public
- HQ
- Newcastle upon tyne, NE128RL, GB, NOVATO, CA
- Founded
- 2024
- Employees
- 2
- Programs
- 201
- Drugs
- 168
- Patents
- 23
miglustat
Approved · small molecule · GM1 Gangliosidoses
miglustat for GM1 Gangliosidoses is a Approved program (small_molecule) at Ultragenyx UK Limited with 1 ClinicalTrials.gov record(s).
Internal code Syner_G_Regimen
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- Ultragenyx UK Limited
- Phase
- Approved
- Modality
- small_molecule
- Indication
- GM1 Gangliosidoses
- Status
- terminated
- Trials
- 1