miglustat
Syner_G_Regimen
Approved small_molecule terminated
Quick answer
miglustat for GM1 Gangliosidoses is a Approved program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Ultragenyx Pharmaceutical
- Indication
- GM1 Gangliosidoses
- Phase
- Approved
- Modality
- small_molecule
- Status
- terminated