Wednesday, July 8, 2026

pharma · Cystic Fibrosis · Multiple Sclerosis · RARE

Ultragenyx UK

UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Bo

Newcastle upon tyne, NE128RL, GB, NOVATO, CA HQ
2024 Founded
2 Employees
Public company Type
RARE · NYSE Ticker
Company details
Status
Public
HQ
Newcastle upon tyne, NE128RL, GB, NOVATO, CA
Founded
2024
Employees
2
Programs
201
Drugs
168
Patents
23
Clinical program

Osilodrostat (Isturisa)

Approved · small molecule · Mild Autonomous Cortisol Secretion (MACS)

Osilodrostat (Isturisa) for Mild Autonomous Cortisol Secretion (MACS) is a Approved program (small_molecule) at Ultragenyx UK Limited with 1 ClinicalTrials.gov record(s).

← All Ultragenyx UK Limited projects Approved small molecule active

Internal code IRB00511675

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Ultragenyx UK Limited
Phase
Approved
Modality
small_molecule
Indication
Mild Autonomous Cortisol Secretion (MACS)
Status
active
Trials
1