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Intelligence · Clinical Pipeline

Ultragenyx UK Pipeline

All ClinicalTrials.gov programs at Ultragenyx UK — phase, modality, and trial IDs.

Programs
201

Quick answer

Ultragenyx UK has 201 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

  1. [6,6-2H2]glucose

    Ultragenyx UK Limited

    Glycogen Storage Disease Type IA

    phase 2 mab completed

    1 trial

  2. allopurinol

    Ultragenyx UK Limited

    Leishmaniasis

    phase 2 small molecule completed

    1 trial

  3. aminomidazole carboxamide riboside

    Ultragenyx UK Limited

    Lesch-Nyhan Syndrome

    phase 2 small molecule completed

    1 trial

  4. anti-thymocyte globulin

    Ultragenyx UK Limited

    Fanconi's Anemia

    phase 2 small molecule completed

    1 trial

  5. anti-thymocyte globulin

    Ultragenyx UK Limited

    Systemic Sclerosis

    phase 2 small molecule completed

    1 trial

  6. arginine butyrate

    Ultragenyx UK Limited

    Beta-Thalassemia

    phase 2 small molecule completed

    1 trial

  7. auranofin

    Ultragenyx UK Limited

    Chronic Lymphocytic Leukemia (CLL)

    phase 2 small molecule completed

    1 trial

  8. bromocriptine

    Ultragenyx UK Limited

    Stereotyped Behavior

    phase 2 small molecule on hold

    1 trial

  9. carbamazepine

    Ultragenyx UK Limited

    Spasms, Infantile

    phase 2 small molecule completed

    1 trial

  10. cidofovir

    Ultragenyx UK Limited

    Cytomegalovirus Retinitis

    phase 2 small molecule completed

    1 trial

  11. cladribine

    Ultragenyx UK Limited

    Cholangitis, Sclerosing

    phase 2 small molecule completed

    1 trial

  12. cyclophosphamide

    Ultragenyx UK Limited

    Pemphigus

    phase 2 small molecule completed

    1 trial

  13. cyclophosphamide

    Ultragenyx UK Limited

    Anemia, Hemolytic, Autoimmune

    phase 2 small molecule completed

    1 trial

  14. cyclosporine

    Ultragenyx UK Limited

    Sickle Cell Anemia

    phase 2 small molecule completed

    1 trial

  15. cytarabine

    Ultragenyx UK Limited

    Lupus Erythematosus, Systemic

    phase 2 small molecule completed

    1 trial

  16. enalapril

    Ultragenyx UK Limited

    Pseudohypoaldosteronism

    phase 2 small molecule completed

    1 trial

  17. fetal nigral transplantation

    Ultragenyx UK Limited

    Parkinson Disease

    phase 2 other completed

    1 trial

  18. filgrastim

    Ultragenyx UK Limited

    Shwachman Syndrome

    phase 2 small molecule completed

    1 trial

  19. fluconazole

    Ultragenyx UK Limited

    Sporotrichosis

    phase 2 small molecule completed

    1 trial

  20. fluconazole

    Ultragenyx UK Limited

    Histoplasmosis

    phase 2 small molecule completed

    1 trial

  21. growth hormone

    Ultragenyx UK Limited

    Cystic Fibrosis

    phase 2 small molecule completed

    1 trial

  22. growth hormone

    Ultragenyx UK Limited

    Turner's Syndrome

    phase 2 small molecule completed

    1 trial

  23. heme arginate

    Ultragenyx UK Limited

    Porphyria

    phase 2 small molecule completed

    3 trials

  24. hydrocortisone

    Ultragenyx UK Limited

    Bronchopulmonary Dysplasia

    phase 2 small molecule completed

    1 trial

  25. irradiation

    Ultragenyx UK Limited

    Brain Neoplasms

    phase 2 other active

    1 trial

  26. itraconazole

    Ultragenyx UK Limited

    Histoplasmosis

    phase 2 small molecule completed

    1 trial

  27. lactulose

    Ultragenyx UK Limited

    Portal Hypertension

    phase 2 small molecule completed

    1 trial

  28. leuprolide

    Ultragenyx UK Limited

    Spinal Muscular Atrophy

    phase 2 small molecule completed

    1 trial

  29. leuprolide

    Ultragenyx UK Limited

    Hyperandrogenism

    phase 2 small molecule completed

    1 trial

  30. leuprolide acetate

    Ultragenyx UK Limited

    Acanthosis Nigricans

    phase 2 small molecule completed

    1 trial

  31. lymphocyte gene therapy

    Ultragenyx UK Limited

    Mucopolysaccharidosis II

    phase 2 gene therapy completed

    1 trial

  32. methoxsalen

    Ultragenyx UK Limited

    Epidermolysis Bullosa Acquisita

    phase 2 small molecule completed

    1 trial

  33. monoclonal factor IX replacement therapy

    Ultragenyx UK Limited

    Hemophilia B

    phase 2 small molecule completed

    1 trial

  34. mucoid exopolysaccharide P. aeruginosa immune globulin IV

    Ultragenyx UK Limited

    Cystic Fibrosis

    phase 2 small molecule completed

    1 trial

  35. octreotide

    Ultragenyx UK Limited

    Hereditary Hemorrhagic Telangiectasia

    phase 2 small molecule completed

    1 trial

  36. olsalazine

    Ultragenyx UK Limited

    Ankylosing Spondylitis

    phase 2 small molecule completed

    1 trial

  37. pallidotomy

    Ultragenyx UK Limited

    Parkinson Disease

    phase 2 other completed

    1 trial

  38. pimozide

    Ultragenyx UK Limited

    Tourette Syndrome

    phase 2 small molecule completed

    1 trial

  39. relaxin

    Ultragenyx UK Limited

    Systemic Sclerosis

    phase 2 small molecule completed

    1 trial

  40. ribose

    Ultragenyx UK Limited

    5'-Nucleotidase Syndrome

    phase 2 small molecule completed

    1 trial

  41. risperidone

    Ultragenyx UK Limited

    Tourette Syndrome

    phase 2 small molecule completed

    1 trial

  42. rituximab

    Ultragenyx UK Limited

    Purpura, Thrombocytopenic, Idiopathic

    phase 2 small molecule completed

    1 trial

  43. scAAV8OTC

    Ultragenyx UK Limited

    Ornithine Transcarbamylase (OTC) Deficiency

    phase 2 gene therapy completed

    1 trial

  44. scAAV9/AGA

    Ultragenyx UK Limited

    Aspartylglucosaminuria

    phase 2 gene therapy active

    1 trial

  45. thalidomide

    Ultragenyx UK Limited

    HIV Infections

    phase 2 small molecule completed

    1 trial

  46. tin mesoporphyrin

    Ultragenyx UK Limited

    Hyperbilirubinemia

    phase 2 small molecule completed

    1 trial

  47. tin mesoporphyrin

    Ultragenyx UK Limited

    Glucosephosphate Dehydrogenase Deficiency

    phase 2 small molecule completed

    1 trial

  48. triheptanoin

    Ultragenyx UK Limited

    Rett Syndrome

    phase 2 small molecule active

    1 trial

Frequently asked questions

How many pipeline programs does Ultragenyx UK have?

201 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.

Data attribution: Data sources · All pipeline programs

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