🇺🇸 FDA
Pipeline program

arginine butyrate

199/15337

Phase 2 small_molecule completed

Quick answer

arginine butyrate for Beta-Thalassemia is a Phase 2 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Beta-Thalassemia
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials