🇺🇸 FDA
Pipeline program

triheptanoin

IRB00085194

Phase 2 small_molecule active

Quick answer

triheptanoin for Rett Syndrome is a Phase 2 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Rett Syndrome
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials