🇺🇸 FDA
Pipeline program

monoclonal factor IX replacement therapy

199/11956

Phase 2 small_molecule completed

Quick answer

monoclonal factor IX replacement therapy for Hemophilia B is a Phase 2 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Hemophilia B
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials