Thursday, July 9, 2026

pharma · Rectal Cancer · Fanconi Anemia · RCKT

Rocket Pharmaceuticals

Rocket Pharmaceuticals is a pharma organization headquartered in Cranbury, USA. It trades on NYSE under ticker RCKT. Primary therapeutic focus areas include Rectal Cancer, Fanconi Anemia, Danon Disease, PKP2 Arrhythmogen

9 Cedarbrook Dr, Cranbury, New Jersey 08512, US HQ
2015 Founded
226 Employees
Public company Type
RCKT · NYSE Ticker
Company details
Status
Public
HQ
9 Cedarbrook Dr, Cranbury, New Jersey 08512, US
Founded
2015
Employees
226
Programs
11
Drugs
10
Patents
1

Quick answer

Rocket Pharmaceuticals is a pharma organization headquartered in Cranbury, USA. It trades on NYSE under ticker RCKT. Primary therapeutic focus areas include Rectal Cancer, Fanconi Anemia, Danon Disease, PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM), Dilated Cardiomyopathy (DCM). NovaPharmaNews links 11 clinical program(s), 1 drug profile(s), and 1 patent record(s) to this entity from public FDA, EMA, ClinicalTrials.gov, and USPTO sources. Pipeline phase mix: phase 1 (4), phase 2 (4), approved (2).

Company snapshot

Rocket Pharma (NASDAQ: RCKT) is a fully-integrated, clinical-stage company seeking gene therapy cures. Rocket places enormous value on people and takes team member progress and well-being just as seriously as the progress and well-being of its pipeline. We are looking for hands-on team players that enjoy collaborating with colleagues who share a passion for our mission and making a difference for

  • 1 approved product(s) across US/EU regulatory metadata.
  • 11 active pipeline program(s) linked via ClinicalTrials.gov.
  • 1 US patent(s) indexed to this assignee profile.

Public regulatory, clinical, patent, and corporate records for Rocket Pharmaceuticals. Not investment advice.

Lead pipeline drugs

Active clinical programs

  • RP-A501 Danon Disease
    Phase 2
  • RP-L102 Fanconi Anemia Complementation Group A
    Phase 2
  • RP-L201 Leukocyte Adhesion Defect - Type I
    Phase 2
  • RP-L301 Pyruvate Kinase Deficiency
    Phase 2

Momentum

Proprietary activity score for Rocket Pharmaceuticals.

1 active signal

20 /100 +0 vs 30 days ago

Signal breakdown

  • Clinical trials 16 30d
  • Nova articles 0 30d
  • Patents filed 0 30d
  • FDA actions 0 30d
  • SEC filings 0 30d
  • Conference presentations 0 90d
  • Pipeline advances 0 30d

Recent activity

Latest pipeline, patent, and corporate events for Rocket Pharmaceuticals.

  1. Clinical update

    RP-A701-0125 — Phase 1

  2. Clinical update

    Clostridium butyricum (live) Tablets(Meiya) — Unknown

  3. Clinical update

    RP-L401 — Phase 1

  4. Clinical update

    RP-L102 — Phase 2

  5. Clinical update

    RP-A601 — Phase 1

View all clinical trial activity →

Quick answers

Common questions about this sponsor — for analysts and search.

  • What is Rocket Pharmaceuticals?

    Rocket Pharmaceuticals is a pharma organization headquartered in Cranbury, USA. It trades on NYSE under ticker RCKT. Primary therapeutic focus areas include Rectal Cancer, Fanconi Anemia, Danon Disease, PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM), Dilated Cardiomyopathy (DCM).

  • Is Rocket Pharmaceuticals publicly traded?

    Yes. Rocket Pharmaceuticals is listed with ticker RCKT on NYSE per SEC EDGAR records linked on this profile.

  • What drugs does Rocket Pharmaceuticals develop or market?

    We link 10 drug profile(s) where Rocket Pharmaceuticals is an originator or marketer in FDA or regional approval metadata. See the drug portfolio table on https://novapharmanews.com/companies/rocket-pharmaceuticals-inc#company-drugs.

  • What are the latest developments for Rocket Pharmaceuticals?

    In the last 12 months our linked public records show 11 trial program update(s) and 0 US patent grant(s) tied to this profile.

  • What therapeutic areas does Rocket Pharmaceuticals focus on?

    Rocket Pharmaceuticals focuses on Rectal Cancer, Fanconi Anemia, Danon Disease based on our analysis of their pipeline programs and drug development activities.

Therapeutic focus

Therapeutic area distribution

Pipeline concentration by therapeutic area from linked clinical programs.

Programs by therapeutic area

Others
16
Cardiology
4
Oncology
3