pharma · Rectal Cancer · Fanconi Anemia · RCKT
Rocket Pharmaceuticals
Rocket Pharmaceuticals B.V.
Rocket Pharmaceuticals is a pharma organization headquartered in Cranbury, USA. It trades on NYSE under ticker RCKT. Primary therapeutic focus areas include Rectal Cancer, Fanconi Anemia, Danon Disease, PKP2 Arrhythmogen
Company details
- Status
- Public
- HQ
- 9 Cedarbrook Dr, Cranbury, New Jersey 08512, US
- Founded
- 2015
- Employees
- 226
- Programs
- 11
- Drugs
- 10
- Patents
- 1
RP-A501
Phase 2 · gene therapy · Danon Disease
RP-A501 for Danon Disease is a Phase 2 program (gene_therapy) at Rocket Pharmaceuticals B.V. with 2 ClinicalTrials.gov record(s).
Internal code RP-A501-0123
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- Rocket Pharmaceuticals B.V.
- Phase
- Phase 2
- Modality
- gene_therapy
- Indication
- Danon Disease
- Status
- active
- Trials
- 2