🇺🇸 FDA
Pipeline program

RP-A601

RP-A601-0323

Phase 1 gene_therapy active

Quick answer

RP-A601 for PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) is a Phase 1 program (gene_therapy) at ROCKET PHARMACEUTICALS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
ROCKET PHARMACEUTICALS, INC.
Indication
PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)
Phase
Phase 1
Modality
gene_therapy
Status
active

Clinical trials