Wednesday, July 8, 2026

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CATALYST PHARMACEUTICALS

CATALYST PHARMACEUTICALS drug portfolio — 20 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

355 Alhambra Circle, Suite 801, Coral Gables, Florida 33134, US HQ
2002 Founded
179 Employees
Public company Type
CPRX · NYSE Ticker
Company details
Status
Public
HQ
355 Alhambra Circle, Suite 801, Coral Gables, Florida 33134, US
Founded
2002
Employees
179
Programs
23
Drugs
20
Patents
61
Intelligence · Drug Pipeline

CATALYST PHARMACEUTICALS pipeline

Portfolio lens on 20 drugs and development assets — regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

CATALYST PHARMACEUTICALS drug portfolio — 20 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

20 compounds
  1. amifampridine

    Nervous system (N07)

    US regulatory status: approved. Molecular target: Voltage-gated potassium channel.

    Target
    Voltage-gated potassium channel
    Mechanism
    Voltage-gated potassium channel blocker
  2. US regulatory status: approved. Molecular target: Voltage-gated potassium channel.

    Target
    Voltage-gated potassium channel
    Mechanism
    Voltage-gated potassium channel blocker
  3. US regulatory status: approved. Molecular target: Sodium-dependent dopamine transporter.

    Target
    Sodium-dependent dopamine transporter
    Mechanism
    Norepinephrine transporter releasing agent
  4. aprocitentan

    Cardiovascular system (C02)

    US regulatory status: approved. Molecular target: Endothelin receptor, ET-A/ET-B.

    Target
    Endothelin receptor, ET-A/ET-B
    Mechanism
    Endothelin receptor, ET-A/ET-B antagonist
  5. US regulatory status: approved. Molecular target: Solute carrier family 12 member 1.

    Target
    Solute carrier family 12 member 1
    Mechanism
    Sodium-(potassium)-chloride cotransporter 2 inhibitor
  6. covid-19 vaccine (inactivated, adjuvanted, adsorbed)

    Antiinfectives for systemic use (J07)

    Antiinfectives for systemic use (J07) compound in CATALYST PHARMACEUTICALS's portfolio. Mechanism: Biological vaccine - induces immune response.

    Mechanism
    Biological vaccine - induces immune response
  7. decitabine

    Antineoplastic and immunomodulating agents (L01)

    US regulatory status: approved. Molecular target: DNA (cytosine-5)-methyltransferase 1.

    Target
    DNA (cytosine-5)-methyltransferase 1
    Mechanism
    DNA (cytosine-5)-methyltransferase 1 inhibitor
  8. dupilumab

    Dermatologicals (D11)

    US regulatory status: approved. Molecular target: Interleukin-4 receptor subunit alpha.

    Target
    Interleukin-4 receptor subunit alpha
    Mechanism
    Interleukin-4 receptor subunit alpha antagonist
  9. eptacog alfa (activated)

    Blood and blood forming organs (B02)

    Blood and blood forming organs (B02) compound in CATALYST PHARMACEUTICALS's portfolio. Molecular target: Coagulation factor VII.

    Target
    Coagulation factor VII
    Mechanism
    Coagulation factor VII exogenous protein
  10. fampridine

    Nervous system (N07)

    Nervous system (N07) compound in CATALYST PHARMACEUTICALS's portfolio. Molecular target: Voltage-gated potassium channel.

    Target
    Voltage-gated potassium channel
    Mechanism
    Voltage-gated potassium channel blocker
  11. Development asset linked to CATALYST PHARMACEUTICALS in public FDA and regional records.

  12. nonacog alfa

    Blood and blood forming organs (B02)

    Blood and blood forming organs (B02) compound in CATALYST PHARMACEUTICALS's portfolio. Molecular target: Coagulation factor IX.

    Target
    Coagulation factor IX
    Mechanism
    Coagulation factor IX exogenous protein
  13. US regulatory status: approved. Molecular target: Copper.

    Target
    Copper
    Mechanism
    Copper chelating agent
  14. Development asset linked to CATALYST PHARMACEUTICALS in public FDA and regional records.

  15. Development asset linked to CATALYST PHARMACEUTICALS in public FDA and regional records.

  16. Development asset linked to CATALYST PHARMACEUTICALS in public FDA and regional records.

  17. US regulatory status: approved. Mechanism: Unknown.

    Mechanism
    Unknown
  18. vamorolone

    Systemic hormonal preparations (H02)

    US regulatory status: approved. Molecular target: Glucocorticoid receptor.

    Target
    Glucocorticoid receptor
    Mechanism
    Mineralocorticoid receptor antagonist
  19. vigabatrin

    Nervous system (N03)

    US regulatory status: approved. Molecular target: 4-aminobutyrate aminotransferase, mitochondrial.

    Target
    4-aminobutyrate aminotransferase, mitochondrial
    Mechanism
    Gamma-amino-N-butyrate transaminase inhibitor