🇺🇸 FDA
Company

CATALYST

CATALYST PHARMACEUTICALS, INC.

CPRX pharma USA

Quick answer

CATALYST is a pharma company (CPRX) headquartered in CORAL GABLES, FL, USA with 23 tracked pipeline programs.

Pipeline (23)

project

Amifampridine Phosphate

Myasthenia Gravis, Generalized

Phase 3 · small_molecule · completed

1 trials
project

Amifampridine Phosphate

Myasthenia Gravis, MuSK

Phase 3 · small_molecule · terminated

1 trials
project

Amifampridine Phosphate

Lambert Eaton Myasthenic Syndrome

Phase 3 · small_molecule · completed

2 trials
project

BT-001

Type2 Diabetes

Phase 3 · other · terminated

1 trials
project

MarzAA

Hemophilia A With Inhibitor

Phase 3 · mab · terminated

1 trials
project

amifampridine phosphate

Myasthenic Syndromes, Congenital

Phase 3 · small_molecule · completed

1 trials
project

Amifampridine Phosphate

Muscular Atrophy, Spinal

Phase 2 · small_molecule · completed

1 trials
project

Amifampridine Phosphate 10 MG Oral Tablet

Spinal Muscular Atrophy Type 3

Phase 2 · small_molecule · terminated

1 trials
project

CPP-109 vigabatrin

Methamphetamine Dependence

Phase 2 · small_molecule · terminated

1 trials
project

Coagulation Factor IX variant

Hemophilia B

Phase 2 · mab · completed

1 trials
project

Coagulation Factor VIIa variant

Factor VII Deficiency

Phase 2 · mab · terminated

1 trials
project

Coagulation Factor VIIa variant

Hemophilia A With Inhibitor

Phase 2 · mab · completed

1 trials
project

Decitabine

Acute Myeloid Leukemia

Phase 2 · small_molecule · active

1 trials
project

Dupilumab

COVID-19

Phase 2 · mab · completed

1 trials
project

MHS-1031

Gastroesophageal Reflux

Phase 2 · small_molecule · active

1 trials
project

vigabatrin

Cocaine Dependence

Phase 2 · small_molecule · completed

2 trials
project

Airway Bypass

Emphysema or COPD

Phase 1 · other · active

1 trials
project

Bumetanide

Seizures

Phase 1 · small_molecule · completed

1 trials
project

CPP-115

Cocaine Dependency

Phase 1 · small_molecule · completed

1 trials
project

HWK-016, MUCIN-16-targeted ADC

PROC

Phase 1 · small_molecule · active

1 trials
project

ISU304/CB2679d/Dalcinonacog alfa 75~150 IU/kg

Hemophilia B

Phase 1 · mab · completed

1 trials
project

MarzAA (marzeptacog alfa [activated])

Hemophilia A

Phase 1 · mab · completed

1 trials
project

PF-05280602

Hemophilia A

Phase 1 · mab · completed

1 trials

Drugs (3)

Patents (8)